Ultra Orphan Assessment

Treatment of patients with molybdenum cofactor deficiency (MoCD) Type A.

Medicine details

Medicine name:
fosdenopterin (Nulibry)
SMC ID:
SMC2624
Pharmaceutical company
Sentynl Therapeutics
BNF chapter
Nutrition and blood
Submission type
Ultra-orphan initial assessment
Publication due date:
09 September 2024
SMC meeting date:
06 August 2024
Patient group submission deadline:
01 July 2024